Cambridge Healthtech Institute’s 4th Annual
RNA-Targeting Small Molecule Drugs
Novel Strategies to Modulate RNA Structure, Binding, Interactions, and Function
APRIL 11 - 12, 2023
With an increased understanding of diverse RNA moieties, their structure, function and interactions, scientists have started exploring small molecules to target RNA, as they offer more stability, oral bioavailability, and have better drug-like properties.
However, identifying the right disease-causing RNA, finding a small molecule to modulate it, and evaluating the downstream physiological responses, can be challenging. Challenges also exist in terms of optimizing the specificity, selectivity, and
safety of these RNA-targeting small molecules in vivo. This conference on RNA-Targeting Small Molecule Drugs will highlight some of the innovative approaches and technologies being used.